Rare Disease Studies - Connecting the Dots - Boston

Discovery Series: Connecting the Dots for Accelerated Rare Disease Studies

Planning and executing a study for a Rare Disease is challenging. Major issues exist involving protocol design, patient recruitment and retention, and global regulatory design.

• Best practices to accelerate these novel compounds to commercialization given difficult rare disease and orphan drug studies
• Special pediatric population issues with Rare Disease studies
• Protocol design, disease epidemiology, patient recruitment, patient retention, and global regulatory design
• Operational efficiencies utilizing experienced, cross functional teams
• Design and maintenance of patient registries for maximum efficiency

Event includes a two hour presentation followed by a cocktail reception including drinks, appetizers and networking.

Parking: Please refer to Medpace Discovery Series for free valet parking.